Progressive engineering of a homing endonuclease genome editing reagent for the murine X-linked immunodeficiency locus

Yupeng Wang(Qingdao University), David J. Rawlings(Center for Infectious Disease Research), David Baker(Howard Hughes Medical Institute), Sandrine Boissel(University of Washington), Andrew M. Scharenberg(CTI BioPharma (Italy)), Joseph Pangallo, Iram Khan, Summer B. Thyme(University of Massachusetts Chan Medical School), Jordan Jarjour(Biogen (United States))
Nucleic Acids Research
March 25, 2014
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