Clinical research for rare disease: Opportunities, challenges, and solutions

Robert C. Griggs(University of Rochester Medical Center), Mark L. Batshaw(Children's National), Mary Dunkle(National Organization for Rare Disorders), Rashmi Gopal-Srivastava(National Institutes of Health), Edward M. Kaye, Jeffrey P. Krischer(University of South Florida), Tan T. Nguyen(United States Food and Drug Administration), Kathleen Paulus(University of South Florida), Peter A. Merkel(Boston University)
Molecular Genetics and Metabolism
November 14, 2008
Cited by 402Open Access
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