Clinical research for rare disease: Opportunities, challenges, and solutions
Robert C. Griggs(University of Rochester Medical Center), Mark L. Batshaw(Children's National), Mary Dunkle(National Organization for Rare Disorders), Rashmi Gopal-Srivastava(National Institutes of Health), Edward M. Kaye, Jeffrey P. Krischer(University of South Florida), Tan T. Nguyen(United States Food and Drug Administration), Kathleen Paulus(University of South Florida), Peter A. Merkel(Boston University)
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