Targeted Disruption of the Acid α-Glucosidase Gene in Mice Causes an Illness with Critical Features of Both Infantile and Adult Human Glycogen Storage Disease Type II

Nina Raben(APT Therapeutics (United States)), Paul H. Plötz(National Institutes of Health), Jerrold M. Ward(National Institutes of Health), Barry J. Byrne(University of Florida Health), Mary E. LaMarca(National Institutes of Health), Brian Sauer(National Institute of Diabetes and Digestive and Kidney Diseases), Laura Lee(National Institutes of Health), Paul Kessler(Johns Hopkins University), Kanneboyina Nagaraju(Children's National), Eunice Lee(National Institute of Arthritis and Musculoskeletal and Skin Diseases), Christina D. King(Buck Institute for Research on Aging)
Journal of Biological Chemistry
July 1, 1998
Cited by 298


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