Propionic acidemia: clinical course and outcome in 55 pediatric and adolescent patients
Sarah C. Grünert(University Medical Center Freiburg), Jörn Oliver Sass(Boston Children's Hospital), Ina Knerr, Sabine Scholl‐Bürgi(Innsbruck Medical University), Claudia M. Haase(Jena University Hospital), Vassiliki Konstantopoulou(Medical University of Vienna), Andrea Superti‐Furga(University of Lausanne), Regina Ensenauer(Zimmer Biomet (Netherlands)), Daniela Karall(Innsbruck Medical University), Matthias R. Baumgartner(University Children's Hospital Zurich), Terttu Suormala(Johns Hopkins University), A. van Teeffelen‐Heithoff(University of Münster), Wolfgang Sperl(Paracelsus Medical University), Jan P. Kraus(Lexicon Pharmaceuticals (United States)), Julia B. Hennermann(Charité - Universitätsmedizin Berlin), Linda De Silva(University Medical Center Freiburg), Robert Steinfeld(University of Göttingen), Thorsten Marquardt(Klinik und Poliklinik für Kinder- und Jugendmedizin), René Santer(Universität Hamburg), Melanie Walter(The University of Sydney), Skadi Beblo(University Hospital Leipzig), Olaf A. Bodamer(Broad Institute), S. Müllerleile(University Medical Center Freiburg), Kerstin Walter(University of Freiburg), Michael Barth(University Medical Center Freiburg), Martin Lindner(Heidelberg University), Karl Otfried Schwab(University Medical Center Freiburg), Thomas Meißner(Düsseldorf University Hospital), Hans-Georg Koch(Klinik und Poliklinik für Kinder- und Jugendmedizin), Michaela Brunner‐Krainz(Graz University Hospital)
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