Early Treatment With Alglucosidase Alfa Prolongs Long-Term Survival of Infants With Pompe Disease
Priya S. Kishnani(Duke University), Deya Corzo, Nancy D. Leslie(Cincinnati Children's Hospital Medical Center), Daniel Gruskin(Emory University), Ans van der Ploeg(Erasmus MC), John Clancy(University of Alabama at Birmingham), Rossella Parini(University of Milano-Bicocca), Gilles Morin(Centre Hospitalier Universitaire Amiens-Picardie), Michael Beck(Universitätskinderklinik), Mislen Bauer(Boston Children's Hospital), Mikaël Jokic(Centre Hospitalier Universitaire de Caen Normandie), Chen-En Tsai(Buddhist Tzu Chi General Hospital), Brian W H Tsai(Chi Mei Medical Center), Claire Morgan, Tara O’Meara, Susan Richards, Elisa Tsao, Hanna Mandel(Rambam Health Care Campus)
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