Measuring patient experiences in Fabry disease: validation of the Fabry-specific Pediatric Health and Pain Questionnaire (FPHPQ)
Uma Ramaswami(The Royal Free Hospital), Catharina Whybra(Johannes Gutenberg University Mainz), Mireia Raluy-Callado(United BioSource Corporation (United Kingdom)), Guillem Pintos‐Morell(Hospital Universitari Germans Trias i Pujol), Gisela Kalkum(Johannes Gutenberg University Mainz), Ingela Wiklund(St George's, University of London), Wen‐Hung Chen, Rossella Parini(MRC Epidemiology Unit), Donald E. Stull(IQVIA (United States)), Marianne Rohrbach(Ghent University Hospital), Michael Beck(Eastern Illinois University)
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