Therapeutic silencing of an endogenous gene by systemic administration of modified siRNAs
Jürgen Soutschek(ALK-Abelló (Germany)), Akin Akinc(Alnylam Pharmaceuticals (United States)), Birgit Bramlage, Klaus Charissé(Alnylam Pharmaceuticals (United States)), Rainer Constien, Mary Donoghue(Alnylam Pharmaceuticals (United States)), Sayda M. Elbashir(Alnylam Pharmaceuticals (United States)), Anke Geick, Philipp Hadwiger, Jens Harborth(Alnylam Pharmaceuticals (United States)), Matthias John, Venkitasamy Kesavan(Alnylam Pharmaceuticals (United States)), Gary Lavine(Alnylam Pharmaceuticals (United States)), Rajendra K. Pandey(Alnylam Pharmaceuticals (United States)), Timothy Racie(Alnylam Pharmaceuticals (United States)), Kallanthottathil G. Rajeev(Alnylam Pharmaceuticals (United States)), Ingo Röhl, Ivanka Toudjarska(Alnylam Pharmaceuticals (United States)), Gang Wang(Alnylam Pharmaceuticals (United States)), Silvio Wuschko, David Bumcrot(Alnylam Pharmaceuticals (United States)), Victor Koteliansky(Alnylam Pharmaceuticals (United States)), Stefan Limmer, Muthiah Manoharan(Alnylam Pharmaceuticals (United States)), Hans‐Peter Vornlocher
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