RNA Toxicity from the ALS/FTD C9ORF72 Expansion Is Mitigated by Antisense Intervention
Christopher J. Donnelly(Johns Hopkins University), Ping‐Wu Zhang(Johns Hopkins University), Jacqueline T. Pham(Johns Hopkins University), Aaron R. Haeusler(Johns Hopkins University), Nipun A. Mistry(Johns Hopkins University), Svetlana Vidensky(Johns Hopkins University), Elizabeth L. Daley(Johns Hopkins University), Erin M. Poth(Johns Hopkins University), Benjamin Hoover(Johns Hopkins University), Daniel M. Fines(Johns Hopkins University), Nicholas J. Maragakis(Johns Hopkins University), Pentti Tienari(University of Helsinki), Leonard Petrucelli(Mayo Clinic in Florida), Bryan J. Traynor(National Institute on Aging), Jiou Wang(Johns Hopkins University), Frank Rigo(Ionis Pharmaceuticals (United States)), C. Frank Bennett(Ionis Pharmaceuticals (United States)), Seth Blackshaw(Johns Hopkins University), Rita Sattler(Johns Hopkins University), Jeffrey D. Rothstein(Johns Hopkins University)
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