Correction of the Enzymatic and Functional Deficits in a Model of Pompe Disease Using Adeno-associated Virus Vectors
Thomas J. Fraites(University of Florida), Barry J. Byrne(University of Florida), Irene Zolotukhin(Florida College), Mary R. Schleissing(Florida College), Paul H. Plötz(National Institutes of Health), Nina Raben(APT Therapeutics (United States)), Scott K. Powers(University of Florida), Glenn Walter(Florida College), Paul Kessler(Johns Hopkins University), R. Andrew Shanely(Appalachian State University), Denise A Cloutier(University of Florida), Daniel Pauly(University of British Columbia)
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