Phase 1 trial of FVIII gene transfer for severe hemophilia A using a retroviral construct administered by peripheral intravenous infusion

Jerry S. Powell(University of North Carolina at Chapel Hill), Deborah Hurst(University of North Carolina at Chapel Hill), Margaret V. Ragni(University of Pittsburgh Medical Center), Veronica Cole(University of North Carolina at Chapel Hill), Douglas J. Jolly(Retriev Technologies (United States)), Sandhya Ramanathan-Girish(University of North Carolina at Chapel Hill), Holger Roehl(University of North Carolina at Chapel Hill), Nancy Sajjadi(University of North Carolina at Chapel Hill), Tom E. Moon(University of North Carolina at Chapel Hill), Gilbert White(University of North Carolina at Chapel Hill), Jeanne M. Lusher(Science Factory), Carol Hillman-Wiseman(University of North Carolina at Chapel Hill)
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