The Pharmacological Chaperone N-butyldeoxynojirimycin Enhances Enzyme Replacement Therapy in Pompe Disease Fibroblasts

Caterina Porto(Federico II University Hospital), Monica Cardone(Telethon Institute Of Genetics And Medicine), Federica Fontana(Federico II University Hospital), Barbara Rossi(Telethon Institute Of Genetics And Medicine), Maria Rosaria Tuzzi(Federico II University Hospital), Antonietta Tarallo(Telethon Institute Of Genetics And Medicine), Maria Vittoria Barone(Federico II University Hospital), Generoso Andria(Federico II University Hospital), Giancarlo Parenti(Federico II University Hospital)
Molecular Therapy
March 17, 2009
10.1038/mt.2009.53
Cited by 149Open Access
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