Enzyme replacement therapy in the mouse model of Pompe disease

Nina Raben(APT Therapeutics (United States)), Paul H. Plötz(National Institutes of Health), Abigail L. Gilbert(National Institute of Arthritis and Musculoskeletal and Skin Diseases), Billy S. Collins, Beth L. Thurberg(Sanofi (United States)), S DWIVEDI(National Institute of Arthritis and Musculoskeletal and Skin Diseases), Robert J. Mattaliano, M. J. Danon(Hennepin County Medical Center), Kanneboyina Nagaraju(Children's National)
Molecular Genetics and Metabolism
September 1, 2003
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