Glycoengineered Acid α-Glucosidase With Improved Efficacy at Correcting the Metabolic Aberrations and Motor Function Deficits in a Mouse Model of Pompe Disease
Yunxiang Zhu(SynZyme Technologies (United States)), Seng H. Cheng(Pfizer (United States)), Ji-Lei Jiang, William M. Canfield(Winthrop-University Hospital), Robin J. Ziegler, Timothy Edmunds, Nathan Gumlaw, Jinhua Zhang(Beijing Jiaotong University), Karen Lee(Mount Sinai Medical Center), Canwen Jiang, Robert J. Mattaliano, Mariko Kudo, Scott D. Bercury(Harvard University)
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