Adeno-associated virus terminal repeat (TR) mutant generates self-complementary vectors to overcome the rate-limiting step to transduction in vivo

Douglas M. McCarty, Haiyan Fu(University of North Carolina at Chapel Hill), Paul E. Monahan(University of North Carolina at Chapel Hill), Charles E. Toulson(Johns Hopkins University), Pooja Naik(University of North Carolina at Chapel Hill), R. Jude Samulski(University of North Carolina at Chapel Hill)
Gene Therapy
November 17, 2003
Cited by 537

Abstract


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