Safety, Tolerability, and Pharmacokinetics of High-Dose Idebenone in Patients With Friedreich Ataxia
Nicholas A. Di Prospero(National Institutes of Health), J. Paul Taylor(St. Jude Children's Research Hospital), Scott Penzak(National Institutes of Health Clinical Center), Kenneth H. Fischbeck(National Institute of Neurological Disorders and Stroke), Bernard Ravina(Voyager Therapeutics (United States)), Charlotte J. Sumner(Johns Hopkins University)
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