Induction and reversal of myotonic dystrophy type 1 pre-mRNA splicing defects by small molecules
Jessica L. Childs‐Disney(Scripps Research Institute), Matthew D. Disney(Scripps Research Institute), Wei Zheng(Liaoning Cancer Hospital & Institute), Noel Southall(National Institutes of Health), Charles A. Thornton(University of Rochester Medical Center), Samarjit Patnaik(National Center for Advancing Translational Sciences), Juan Marugán(National Institutes of Health), George C. Schatz(Northwestern University), Krzysztof Sobczak(Adam Mickiewicz University in Poznań), Ilyas Yildirim(Florida Atlantic University), HaJeung Park(Scripps Research Institute), Jason W. Hoskins(University of Rochester), Tuan Anh Tran(Johns Hopkins University), Catherine Z. Chen(National Institutes of Health), Chris Austin(National Institutes of Health), Ewa Stępniak-Konieczna(Adam Mickiewicz University in Poznań)
Cited by 95
Related Papers
Present and Future of Surface-Enhanced Raman Scattering
|ACS Nano|2019|3.7k
Energy landscapes and functions of supramolecular systems
|Nature Materials|2016|462
Human Pluripotent Stem Cell-Derived Neural Cells and Brain Organoids Reveal SARS-CoV-2 Neurotropism Predominates in Choroid Plexus Epithelium
|Cell stem cell|2020|460
Unexplored therapeutic opportunities in the human genome
|Nature Reviews Drug Discovery|2018|391