Transplantation of Genetically Corrected Human iPSC-Derived Progenitors in Mice with Limb-Girdle Muscular Dystrophy

Francesco Saverio Tedesco(MRC Laboratory for Molecular Cell Biology), Giulio Cossu(Vita-Salute San Raffaele University), Federica Ungaro(IRCCS Ospedale San Raffaele), Rossana Tonlorenzi(Baylor College of Medicine), Marco Cassano, Laura Perani(Vita-Salute San Raffaele University), Vania Broccoli(Vita-Salute San Raffaele University), Ornella Cappellari(Vita-Salute San Raffaele University), Peter Schneiderat(Evangelisches Krankenhaus Bielefeld), Benedikt Schoser(Friedrich Baur Stiftung), M Gerli(Great Ormond Street Hospital), Roberto Bottinelli(University of Pavia), Martina Ragazzi(Vita-Salute San Raffaele University), Emanuela Longa(University of Pavia), Giorgia Calderazzi(Vita-Salute San Raffaele University), Sara Benedetti(Vita-Salute San Raffaele University), Enrico Tagliafico(University of Modena and Reggio Emilia), Maurilio Sampaolesi(Sapienza University of Rome), Marina Mora(Fondazione IRCCS Istituto Neurologico Carlo Besta), Hidetoshi Hoshiya(Vita-Salute San Raffaele University), Mitsuo Oshimura(Tottori University), Yvan Torrente(University of Milan), Stefania Antonini(Vita-Salute San Raffaele University), Valentina Artusi(University of Modena and Reggio Emilia)
Science Translational Medicine
June 27, 2012
Cited by 293


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