Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology
J. Alter(Hammersmith Hospital), Fang Lou(University of Hertfordshire), Adam Rabinowitz(Hammersmith Hospital), HaiFang Yin(Hammersmith Hospital), Jeffrey Rosenfeld(Carolinas Medical Center), Steve D. Wilton(University of Western Australia), Terence A. Partridge(Hammersmith Hospital), Qi Long Lu(Muscular Dystrophy Association)
Cited by 492
Abstract
Related Papers
No related papers found
Powered by citation graph analysis