Reengineering a receptor footprint of adeno-associated virus enables selective and systemic gene transfer to muscle

Aravind Asokan(University of North Carolina at Chapel Hill), Julia C Conway(University of North Carolina at Chapel Hill), Jana L. Phillips(University of North Carolina at Chapel Hill), Chengwen Li(University of North Carolina at Chapel Hill), Julia Hegge(Mirus Bio (United States)), Rebecca Sinnott(University of North Carolina at Chapel Hill), Swati Yadav(University of North Carolina at Chapel Hill), Nina DiPrimio(University of North Carolina at Chapel Hill), Hyun Joo Nam(University of Florida), Mavis Agbandje‐McKenna(University of Florida), Scott McPhee(AskBio (United States)), Jon A. Wolff(Mirus Bio (United States)), R. Jude Samulski(University of North Carolina at Chapel Hill)
Nature Biotechnology
December 27, 2009
Cited by 259Open Access
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