Efficient Hepatic Delivery and Expression from a Recombinant Adeno-associated Virus 8 Pseudotyped α1-Antitrypsin Vector

Thomas J. Conlon(Adelson Foundation), Terence R. Flotte(University of Massachusetts Chan Medical School), Travis Cossette(University of Florida), Tracy Clarke(University of Florida), Kirsten Erger(University of Florida), Marda Scott-Jorgensen(University of Florida), Martha Campbell‐Thompson(University of Florida), James M. Crawford(Northwell Health), Young‐Kook Choi(University of Florida), Sihong Song(American Association of Colleges of Pharmacy)
Molecular Therapy
August 9, 2005
10.1016/j.ymthe.2005.05.016
Cited by 56

Related Papers

Treatment of Leber Congenital Amaurosis Due to <i>RPE65</i> Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results of a Phase I Trial
|Human Gene Therapy|2008|950
Nanodroplet processing platform for deep and quantitative proteome profiling of 10–100 mammalian cells
|Nature Communications|2018|629
Marked Expansion of Exocrine and Endocrine Pancreas With Incretin Therapy in Humans With Increased Exocrine Pancreas Dysplasia and the Potential for Glucagon-Producing Neuroendocrine Tumors
|Diabetes|2013|455
Heme Oxygenase-1 Modulates Early Inflammatory Responses
|American Journal Of Pathology|2004|416
Recombinant Adeno-Associated Virus Serotype 9 Leads to Preferential Cardiac Transduction In Vivo
|Circulation Research|2006|400