Gel-mediated Delivery of AAV1 Vectors Corrects Ventilatory Function in Pompe Mice With Established Disease

Cathryn Mah(Anna Needs Neuroblastoma Answers), Barry J. Byrne(University of Florida), Jeffry S. Kelley(University of Florida), Kerry O. Cresawn(University of Florida), Darin J. Falk, David D. Fuller(Brenau University), Sean Germain(University of Florida), Thomas J. Fraites(University of Florida), Melissa A. Lewis(The University of Texas at Arlington), Lara R. DeRuisseau(University of Florida), Martha Campbell‐Thompson(University of Florida), Denise A Cloutier(University of Florida), Thomas J. Conlon(Adelson Foundation)
Molecular Therapy
January 26, 2010
10.1038/mt.2009.305
Cited by 76

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