Intrathecal enzyme replacement therapy: Successful treatment of brain disease via the cerebrospinal fluid
Patricia Dickson(Barnes-Jewish Hospital), Emil Kakkis(Johannes Gutenberg University Mainz), Merry Passage(The Lundquist Institute), Maryn Peinovich(UCLA Medical Center), Beth Levy(Saint Louis University), Carole Vogler(University of Washington), Steven Q. Le(UCLA Medical Center), Stephen R. Hanson(Oregon Health & Science University), Michael F. McEntee(Knoxville College)
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