Long-term gene expression and phenotypic correction using adeno-associated virus vectors in the mammalian brain
Michael G. Kaplitt(Yale University), Paola Leone(Yale University), R. Jude Samulski(University of North Carolina at Chapel Hill), Xiao Xiao, Donald W. Pfaff(Rockefeller University), Karen L. O’Malley(Washington University in St. Louis), Matthew J. During(Yale University)
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