Reversal of Blindness in Animal Models of Leber Congenital Amaurosis Using Optimized AAV2-mediated Gene Transfer
Jeannette Bennicelli(University of Pennsylvania), J. Fraser Wright(Children's Hospital of Philadelphia), András M. Komáromy(University of Pennsylvania), Jonathan B. Jacobs(Case Western Reserve University), Bernd Hauck(Children's Hospital of Philadelphia), Olga Zelenaia(Children's Hospital of Philadelphia), Federico Mingozzi(Children's Hospital of Philadelphia), Daniel J. Hui(Children's Hospital of Philadelphia), Daniel C. Chung(Penn Presbyterian Medical Center), Tonia S. Rex(University of Pennsylvania), Zhangyong Wei(University of Pennsylvania), Guang Qu(Children's Hospital of Philadelphia), Shangzhen Zhou(Children's Hospital of Philadelphia), Caroline J. Zeiss(Yale University), Valder R. Arruda(Children's Hospital of Philadelphia), Gregory M. Acland(Cornell University), Lou F Dell'Osso(Case Western Reserve University), Katherine A. High(Children's Hospital of Philadelphia), Albert M. Maguire(Penn Presbyterian Medical Center), Jean Bennett(Penn Presbyterian Medical Center)
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