Large-scale screening using familial dysautonomia induced pluripotent stem cells identifies compounds that rescue IKBKAP expression
Gabsang Lee(Johns Hopkins University), Christina N. Ramirez(Kettering University), Hyesoo Kim(Johns Hopkins University), Nadja Zeltner(Kettering University), Becky Liu(Kettering University), Constantin Radu(Kettering University), Bhavneet Bhinder(Kettering University), Yong Jun Kim(Johns Hopkins University), In Young Choi(Johns Hopkins Medicine), Bipasha Mukherjee-Clavin(Johns Hopkins Medicine), Hakim Djaballah(Kettering University), Lorenz Studer(Kettering University)
Cited by 226Open Access
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