Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-α-glucosidase
Andrea Amalfitano(National Institutes of Health), Yuting Chen(National Institutes of Health), Nina Raben(APT Therapeutics (United States)), Thomas L. Dawson(Agency for Science, Technology and Research), Hao Hu(National Institutes of Health), Alison McVie‐Wylie, Paul H. Plötz(National Institutes of Health)
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