An RNAi therapeutic targeting antithrombin to rebalance the coagulation system and promote hemostasis in hemophilia

Alfica Sehgal(Alnylam Pharmaceuticals (United States)), Scott Barros(Alnylam Pharmaceuticals (United States)), Lacramioara Ivanciu(Children's Hospital of Philadelphia), Brian C. Cooley(University of North Carolina at Chapel Hill), June Qin(Alnylam Pharmaceuticals (United States)), Tim Racie(Alnylam Pharmaceuticals (United States)), Julia Hettinger(Alnylam Pharmaceuticals (United States)), Mary Carioto(Alnylam Pharmaceuticals (United States)), Yongfeng Jiang(Alnylam Pharmaceuticals (United States)), Josh Brodsky(Alnylam Pharmaceuticals (United States)), Harsha Prabhala(Alnylam Pharmaceuticals (United States)), Xuemei Zhang(Alnylam Pharmaceuticals (United States)), Husain Attarwala(Alnylam Pharmaceuticals (United States)), Renta Hutabarat(Alnylam Pharmaceuticals (United States)), Don Foster(Alnylam Pharmaceuticals (United States)), Stuart Milstein(Alnylam Pharmaceuticals (United States)), Klaus Charissé(Alnylam Pharmaceuticals (United States)), Satya Kuchimanchi(Alnylam Pharmaceuticals (United States)), Martin A. Maier(Alnylam Pharmaceuticals (United States)), Lubo Nechev(Alnylam Pharmaceuticals (United States)), Kandasamy Pachamuthu(Alnylam Pharmaceuticals (United States)), Alexander V. Kel’in(Alnylam Pharmaceuticals (United States)), Jayaprakash K. Nair(Alnylam Pharmaceuticals (United States)), Kallanthottathil G. Rajeev(Alnylam Pharmaceuticals (United States)), Muthiah Manoharan(Alnylam Pharmaceuticals (United States)), Rachel Meyers(Alnylam Pharmaceuticals (United States)), Benny Sørensen(Alnylam Pharmaceuticals (United States)), Amy Simon(Alnylam Pharmaceuticals (United States)), Yesim Dargaud(Université Claude Bernard Lyon 1), Claude Négrier(Université Claude Bernard Lyon 1), Rodney M. Camire(Children's Hospital of Philadelphia), Akin Akinc(Alnylam Pharmaceuticals (United States))
Nature Medicine
April 7, 2015
Cited by 296

Abstract


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