Three-Year Follow-up after Unilateral Subretinal Delivery of Adeno-Associated Virus in Patients with Leber Congenital Amaurosis Type 2
Francesco Testa(University of Naples Federico II), Albert M. Maguire(Children's Hospital of Philadelphia), Settimio Rossi(University of Naples Federico II), Eric A. Pierce(University of Pennsylvania), Paolo Melillo(University of Campania "Luigi Vanvitelli"), Kathleen Marshall(Children's Hospital of Philadelphia), Sandro Banfi(Telethon Institute Of Genetics And Medicine), Enrico Maria Surace(Telethon Institute Of Genetics And Medicine), Junwei Sun(University of Pennsylvania), Carmela Acerra(University of Campania "Luigi Vanvitelli"), J. Fraser Wright(Children's Hospital of Philadelphia), Jennifer Wellman(Children's Hospital of Philadelphia), Katherine A. High(Howard Hughes Medical Institute), Alberto Auricchio(Telethon Institute Of Genetics And Medicine), Jean Bennett(University of Pennsylvania), Francesca Simonelli(University of Campania "Luigi Vanvitelli")
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