Sustained Reduction of Hyperbilirubinemia in Gunn Rats After Adeno-Associated Virus-Mediated Gene Transfer of Bilirubin UDP-Glucuronosyltransferase Isozyme 1A1 to Skeletal Muscle
Nunzia Pastore(Telethon Institute Of Genetics And Medicine), Nicola Brunetti‐Pierri(Federico II University Hospital), Rosa Maria Sepe(Telethon Institute Of Genetics And Medicine), Edoardo Nusco(Telethon Institute Of Genetics And Medicine), Francesco Vetrini(Indiana University – Purdue University Indianapolis), Libor Vı́tek(Charles University), Alberto Auricchio(Federico II University Hospital), Jana Vaníková(Charles University), Antony F. McDonagh(University of California, San Francisco)
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