Intrathecal enzyme replacement therapy reduces lysosomal storage in the brain and meninges of the canine model of MPS I

Emil Kakkis(BioMarin (United States)), Merry Passage(University of California, Los Angeles), Patricia Dickson(Washington University in St. Louis), Michael F. McEntee(Knoxville College), Pavel V. Belichenko(Stanford University), Si-Hung Le(UCLA Medical Center), Beth Levy(Saint Louis University), Carole Vogler(University of Washington), Stephen R. Hanson(Oregon Health & Science University), William C. Mobley(University of California San Diego)
Molecular Genetics and Metabolism
August 27, 2004
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