Biochemical Correction of Short-Chain Acyl-Coenzyme A Dehydrogenase Deficiency After Portal Vein Injection of rAAV8-SCAD
Stuart G. Beattie(University of Massachusetts Chan Medical School), Terence R. Flotte(University of Massachusetts Chan Medical School), Jerry Vockley(Pittsburgh Public Schools), Sean Germain(University of Florida), Dietrich Matern(Mayo Clinic), Glenn A. Walter(University of Florida), Eric S. Goetzman(Pediatrics and Genetics), Martha Campbell‐Thompson(University of Florida), Thomas J. Conlon(Adelson Foundation)
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