EPI-743 reverses the progression of the pediatric mitochondrial disease—Genetically defined Leigh Syndrome
Diego Martinelli(Bambino Gesù Children's Hospital), Michela Catteruccia, Fiorella Piemonte, Anna Pastore(Bambino Gesù Children's Hospital), Giulia Tozzi, Carlo Dionisi‐Vici(Bambino Gesù Children's Hospital), Giuseppe Pontrelli, Tiziana Corsetti, Susanna Livadiotti, Viktoria Kheifets(Edison Pharmaceuticals (United States)), A. Scott Hinman(Edison Pharmaceuticals (United States)), William D. Shrader(Edison Pharmaceuticals (United States)), Martin Thoolen(Edison Pharmaceuticals (United States)), Matthew B. Klein(Edison Pharmaceuticals (United States)), Enrico Bertini, Guy Miller(Edison Pharmaceuticals (United States))
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