Aberrant splicing in the ocular albinism type 1 gene (OA1/GPR143) is corrected in vitro by morpholino antisense oligonucleotides
Francesco Vetrini(Indiana University – Purdue University Indianapolis), Valeria Marigo(University of Modena and Reggio Emilia), Michele De Luca(University of Modena and Reggio Emilia), Roberta Tammaro(Telethon Institute Of Genetics And Medicine), Andrea Ballabio(Baylor College of Medicine), Alberto Auricchio(Federico II University Hospital), Enrico Maria Surace(Telethon Institute Of Genetics And Medicine), Sergio Bondanza(Istituto Dermopatico dell'Immacolata)
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