Substrate reduction therapy in juvenile GM2 gangliosidosis
Gustavo Maegawa(Johns Hopkins Medicine), Joe T.R. Clarke(Dalhousie University), Susan Blasér(University of Toronto), Maggie E. Toplak(York University), Jason Hayes(University of Toronto), Cynthia Hawkins(Hospital for Sick Children), Brenda Banwell(Johns Hopkins University), Cameron Ackerley(University of Toronto), G Sorge(York University)
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