Hepatocytes corrected by gene therapy are selected in vivo in a murine model of hereditary tyrosinaemia type I

Ken Overturf(Oregon Health & Science University), Muhsen Al-Dhalimy(Oregon Health & Science University), Robert M. Tanguay(Université Laval), Mark Brantly(National Institutes of Health), Ching-Nan Ou(Texas Children's Hospital), Milton J. Finegold(Texas Children's Hospital), Markus Grompe(Oregon Health & Science University)
Nature Genetics
March 1, 1996
Cited by 555

Abstract


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