Targeted genome editing in human repopulating haematopoietic stem cells

Pietro Genovese(The San Raffaele Telethon Institute for Gene Therapy), Giulia Schiroli(Vita-Salute San Raffaele University), Giulia Escobar(The San Raffaele Telethon Institute for Gene Therapy), Tiziano Di Tomaso(The San Raffaele Telethon Institute for Gene Therapy), Claudia Firrito(The San Raffaele Telethon Institute for Gene Therapy), Andrea Calabria(The San Raffaele Telethon Institute for Gene Therapy), Davide Moi(The San Raffaele Telethon Institute for Gene Therapy), Roberta Mazzieri(The San Raffaele Telethon Institute for Gene Therapy), Chiara Bonini(San Raffaele University of Rome), Michael C. Holmes(Sangamo BioSciences (United States)), Philip D. Gregory(Sangamo BioSciences (United States)), Mirjam van der Burg(Erasmus MC), Bernhard Gentner(The San Raffaele Telethon Institute for Gene Therapy), Eugenio Montini(The San Raffaele Telethon Institute for Gene Therapy), Angelo Lombardo(Vita-Salute San Raffaele University), Luigi Naldini(Vita-Salute San Raffaele University)
Nature
May 28, 2014
Cited by 564Open Access
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