Antisense-Oligonucleotide Mediated Exon Skipping in Activin-Receptor-Like Kinase 2: Inhibiting the Receptor That Is Overactive in Fibrodysplasia Ossificans Progressiva

Songting Shi(Leiden University Medical Center), Peter ten Dijke(Leiden University Medical Center)
PLoS ONE
July 4, 2013
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