Lentiviral Vector-Mediated Gene Transfer in T Cells from Wiskott–Aldrich Syndrome Patients Leads to Functional Correction
Loı̈c Dupré(The San Raffaele Telethon Institute for Gene Therapy), Maria‐Grazia Roncarolo(Regenerative Medicine Institute), António Bernad(Spanish National Centre for Cardiovascular Research), Claudio Bordignon(Vita-Salute San Raffaele University), Alessandro Aiuti(San Raffaele University of Rome), Sara Trifari(The San Raffaele Telethon Institute for Gene Therapy), Antonia Follenzi(Università degli Studi del Piemonte Orientale “Amedeo Avogadro”), Luigi Naldini(University of Turin), Francesco Marangoni(Vita-Salute San Raffaele University), Silvana Di Martino(University of Turin), Shigeru Tsuchiya(Tohoku University), Teresa Laı́n de Lera(Centro Nacional de Biotecnología)
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