Lentiviral Vector-Mediated Gene Transfer in T Cells from Wiskott–Aldrich Syndrome Patients Leads to Functional Correction
Loı̈c Dupré(The San Raffaele Telethon Institute for Gene Therapy), Maria‐Grazia Roncarolo(Vita-Salute San Raffaele University), António Bernad(Centro Nacional de Biotecnología), Claudio Bordignon(Vita-Salute San Raffaele University), Alessandro Aiuti(University of Rome Tor Vergata), Sara Trifari(The San Raffaele Telethon Institute for Gene Therapy), Antonia Follenzi(Università degli Studi del Piemonte Orientale “Amedeo Avogadro”), Luigi Naldini(Vita-Salute San Raffaele University), Francesco Marangoni(Vita-Salute San Raffaele University), Silvana Di Martino(University of Turin), Shigeru Tsuchiya(Tohoku University), Teresa Laı́n de Lera(Centro Nacional de Biotecnología)
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