Differences in the predominance of lysosomal and autophagic pathologies between infants and adults with Pompe disease: implications for therapy

Nina Raben(APT Therapeutics (United States)), Paul H. Plötz(National Institutes of Health), Wuh‐Liang Hwu(National Taiwan University Hospital), Rebecca Baum(National Institutes of Health), Cynthia Schreiner(National Institutes of Health), Yin‐Hsiu Chien(National Taiwan University Hospital), Evelyn Ralston(National Institutes of Health), Kristien J.M. Zaal(National Institutes of Health)
Molecular Genetics and Metabolism
August 8, 2010
Cited by 74


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