Towards a therapy for Angelman syndrome by targeting a long non-coding RNA

Linyan Meng(Baylor Genetics), Frank Rigo(Ionis Pharmaceuticals (United States)), Arthur L. Beaudet(Lunar and Planetary Institute), Seung Chun(Ionis Pharmaceuticals (United States)), C. Frank Bennett(Pennsylvania State University), Amanda J. Ward(Ionis Pharmaceuticals (United States))
Nature
December 1, 2014
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