Targeted gene correction of α1-antitrypsin deficiency in induced pluripotent stem cells

Kosuke Yusa(Wellcome Sanger Institute), S. Tamir Rashid(University of Cambridge), Hélène Strick‐Marchand(Institut Pasteur), Ignacio Varela(Instituto de Biomedicina y Biotecnología de Cantabria), Pei-Qi Liu(Sangamo BioSciences (United States)), David E. Paschon(Sangamo BioSciences (United States)), Elena Miranda(Wellcome Trust), A. Ordóñez(Wellcome Trust), Nicholas R. F. Hannan(University of Cambridge), Foad J. Rouhani(University of Cambridge), Sylvie Darche(Inserm), Graeme Alexander(Cambridge University Hospitals NHS Foundation Trust), Stefan J. Marciniak(University of Cambridge), Noemi Fusaki(ID Pharma (Japan)), Mamoru Hasegawa(ID Pharma (Japan)), Michael C. Holmes(Sangamo BioSciences (United States)), James P. Di Santo(Inserm), David A. Lomas(University of Cambridge), Allan Bradley(Wellcome Sanger Institute), Ludovic Vallier(University of Cambridge)
Nature
October 11, 2011
Cited by 640Open Access
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