Systemic Correction of a Fatty Acid Oxidation Defect by Intramuscular Injection of a Recombinant Adeno-Associated Virus Vector
Thomas J. Conlon(Adelson Foundation), Terence R. Flotte(University of Massachusetts Chan Medical School), Jerry Vockley(Pittsburgh Public Schools), Dietrich Matern(Mayo Clinic), Glenn A. Walter(University of Florida), Kirsten Erger(University of Florida), Renius Owen(University of Florida Health), Gregory M. Gutierrez(ID Genomics (United States)), Eric S. Goetzman(Pediatrics and Genetics), Travis Cossette(University of Florida)
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