Safe, Efficient, and Reproducible Gene Therapy of the Brain in the Dog Models of Sanfilippo and Hurler Syndromes
N. Matthew Ellinwood(Iowa State University), Jérôme Ausseil(Inserm), Nathalie Desmaris(Inserm), Stéphanie Bigou(Inserm), Song Liu(Inserm), Jackie K. Jens(Iowa State University), Elizabeth Snella(Iowa State University), Eman EA Mohammed(Iowa State University), Chris Thomson(Iowa State University), Sylvie Raoul(Hôpital Nord), Béatrice Joussemet(Oniris), Françoise Roux(Oniris), Yan Chérel(Oniris), Y Lajat(Hôpital Nord), Monique Piraud, Rachid Benchaouir(AIMM Therapeutics (Netherlands)), Stephan Hermening(AIMM Therapeutics (Netherlands)), Harald Petry(AIMM Therapeutics (Netherlands)), Roseline Froissart, Marc Tardieu(Inserm), Carine Ciron(Inserm), Philippe Moullier(Inserm), J. Parkes(Iowa State University), Karen L. Kline(Iowa State University), Irène Maire, Marie‐Thérèse Vanier(Inserm), Jean‐Michel Heard(Inserm), Marie-Anne Colle(Oniris)
Cited by 137Open Access
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