Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery

Angelo Lombardo(The San Raffaele Telethon Institute for Gene Therapy), Pietro Genovese(The San Raffaele Telethon Institute for Gene Therapy), Christian Beauséjour(Sangamo BioSciences (United States)), Silvia Colleoni(Istituto Sperimentale Italiano Lazzaro Spallanzani), Ya-Li Lee(Sangamo BioSciences (United States)), Kenneth A Kim(Sangamo BioSciences (United States)), Dale Ando(Sangamo BioSciences (United States)), Fyodor D. Urnov(Sangamo BioSciences (United States)), Cesare Galli(Istituto Sperimentale Italiano Lazzaro Spallanzani), Philip D. Gregory(Sangamo BioSciences (United States)), Michael C. Holmes(Sangamo BioSciences (United States)), Luigi Naldini(Vita-Salute San Raffaele University)
Nature Biotechnology
October 28, 2007
Cited by 840

Abstract


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