Correction of Neurological Disease of Mucopolysaccharidosis IIIB in Adult Mice by rAAV9 Trans-Blood–Brain Barrier Gene Delivery
Haiyan Fu(Nationwide Children's Hospital), Julianne DiRosario(Nationwide Children's Hospital), Smruti Killedar(Nationwide Children's Hospital), Kimberly Zaraspe(Nationwide Children's Hospital), Douglas M. McCarty(Nationwide Children's Hospital)
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