Correction of Neurological Disease of Mucopolysaccharidosis IIIB in Adult Mice by rAAV9 Trans-Blood–Brain Barrier Gene Delivery

Haiyan Fu(Nationwide Children's Hospital), Julianne DiRosario(Nationwide Children's Hospital), Smruti Killedar(Nationwide Children's Hospital), Kimberly Zaraspe(Nationwide Children's Hospital), Douglas M. McCarty(Nationwide Children's Hospital)
Molecular Therapy
March 8, 2011
Cited by 197Open Access
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