Osteopetrosis rescue upon RANKL administration to <i>Rankl</i>−<i>/</i>− mice: A new therapy for human RANKL-dependent ARO
Nadia Lo Iacono(Institute of Genetic and Biomedical Research), Cristina Sobacchi(Humanitas University), Matteo M. Guerrini(Fondazione Humanitas per la Ricerca), Barbara Cassani(Humanitas University), Veronica Marrella(Humanitas University), Elena Fontana(Institute of Genetic and Biomedical Research), Stefano Mantero(Humanitas University), Alessandra Pangrazio(Institute of Biomedical Technologies), Marianna Paulis(Humanitas University), Paolo Vezzoni(Humanitas University), Pietro Luigi Poliani(University of Brescia), Paul J. Kostenuik(Amgen (United States)), Elisabetta Traggiai, Harry C. Blair(University of Pittsburgh Medical Center), Virginia Maina(Humanitas University), Fabio Facchetti(University of Brescia), Anna Villa(Institute of Genetic and Biomedical Research), Laura Crisafulli(Humanitas University), Antonio Inforzato(Humanitas University), Francesca Schena, Serenella Valaperta(Humanitas University), Francesca Ficara(Humanitas University)
Cited by 54
Related Papers
International Consensus Classification of Myeloid Neoplasms and Acute Leukemias: integrating morphologic, clinical, and genomic data
|Blood|2022|2.7k
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency
|New England Journal of Medicine|2009|1k
Osteopetrosis: genetics, treatment and new insights into osteoclast function
|Nature Reviews Endocrinology|2013|580
Osteoblast Differentiation and Bone Matrix Formation <i>In Vivo</i> and <i>In Vitro</i>
|Tissue Engineering Part B Reviews|2016|471
Osteoclast-poor human osteopetrosis due to mutations in the gene encoding RANKL
|Nature Genetics|2007|387