Targeted Correction of the Point Mutations of β-Thalassemia and Targeted Mutagenesis of the Nucleotide Associated with HPFH by RNA/DNA Oligonucleotides: Potential for β-Thalassemia Gene Therapy

Zhu‐Hong Li(Chinese Academy of Medical Sciences & Peking Union Medical College), Chih‐Chuan Liang(Chinese Academy of Medical Sciences & Peking Union Medical College), De‐Pei Liu(Chinese Academy of Medical Sciences & Peking Union Medical College), Zhi-Chen Guo(Chinese Academy of Medical Sciences & Peking Union Medical College), Wenxuan Yin(Tongji University)
Blood Cells Molecules and Diseases
March 1, 2001
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