Human CD34+ hematopoietic progenitor cell-directed lentiviral-mediated gene therapy in a xenotransplantation model of lysosomal storage disease
A. Alex Hofling(Washington University in St. Louis), Steven M. Devine(Washington University in St. Louis), Carole Vogler(Saint Louis University), Mark S. Sands(Washington University in St. Louis)
Cited by 46Open Access
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