Enzyme augmentation therapy enhances the therapeutic efficacy of bone marrow transplantation in mucopolysaccharidosis type II mice

Kazumasa Akiyama(Jikei University School of Medicine), Toya Ohashi(Jikei University School of Medicine), Brett E. Crawford(BioMarin (United States)), Jillian R. Brown(APC Microbiome Institute), Hiromitsu Nakauchi(University of Tsukuba), Takashi Higuchi(Kyoto University), Yohta Shimada(Jikei University School of Medicine), Yoshikatsu Eto(Advanced Medical Research Institute), Makoto Ohtsu(Tokyo University of Science), Hiroshi Kobayashi(Jikei University School of Medicine), Takahiro Fukuda(Takarazuka City Hospital), Hiroyuki Ida(Fujieda Municipal General Hospital)
Molecular Genetics and Metabolism
September 22, 2013
Cited by 16


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