Visualizing lipid-formulated siRNA release from endosomes and target gene knockdown
Anders Wittrup(Lund University), Angela Ai(Boston Children's Hospital), Xing Liu(Boston Children's Hospital), Péter Hamar(Semmelweis University), Radiana Trifonova(Boston Children's Hospital), Klaus Charissé(Alnylam Pharmaceuticals (United States)), Muthiah Manoharan(Alnylam Pharmaceuticals (United States)), Tomas Kirchhausen(Boston Children's Hospital), Judy Lieberman(Boston Children's Hospital)
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Abstract
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